Patients in the #US with #SanfilipposyndrometypeA have their first #FDA-approved treatment, #UltragenyxPharma's #genetherapy #Fayuvi, which will launch with a $3.9 million price tag.
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@pharmaphorum.bsky.socialPatients in the #US with #SanfilipposyndrometypeA have their first #FDA-approved treatment, #UltragenyxPharma's #genetherapy #Fayuvi, which will launch with a $3.9 million price tag.