Andelyn Achieves Groundbreaking FDA Approval for Gene Therapy Manufacturing Milestone #United_States #Columbus #Andelyn_Biosciences #FAYUVI #MPS_IIIA

Patients in the #US with #SanfilipposyndrometypeA have their first #FDA-approved treatment, #UltragenyxPharma's #genetherapy #Fayuvi, which will launch with a $3.9 million price tag.

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