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@yoshitakahoshi.bsky.socialSep 11, 2026, 11:10 PM

軟骨無形成低身長症へのVOXZOGO第3相結果をBioMarinが発表──NEJM Evidence掲載、FDA申請の根拠データを整理
stellanews.life/technology/1... #CANOPY-HCH-3 #vosoritide

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