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@4040rec.bsky.socialOct 7, 2026, 10:48 AM

#pharmaceuticals #SOBI #NICE #Tryngolza #olezarsen #FCStreatment #NICEGuidance #NICEfinaldraftguidance #England #Wales #familialchylomicronaemiasyndrome #triglycerideloweringtreatments #ultrararediseases #inheritedlipiddisorder #hypertriglyceridaemia #Balancestudy #FCScommunity #NHS
zurl.co/7AC7l

@4040rec.bsky.socialOct 5, 2026, 10:10 AM

#pharma #pharmaceuticals #NICE #desmoidtumours #NICEApproval #patientaccess #Merck #NICEfinaldraftguidance #Ogsiveo #England #NHS #CancerDrugsFund #nirogacestat #targeteddrugtreatment #rarecancer #softtissuetumours #DesmoidAidUK #DeFitrial #RareTumours #innovativemedicines
zurl.co/iM0Ds

@4040rec.bsky.socialSep 21, 2026, 8:54 AM

#NICE #JnJ #Haematology #multiplemyeloma #daratumumab #daratumumabquadruplet #transplanteligiblemyeloma #NICEGuidance #MRDguidedtreatment #NICEFinalDraftGuidance #PERSEUSdata #daratumumabbasedregimen #VRdinduction #MRDguidedapproach #personalisedtreatment #PatientAccess
zurl.co/ZmXyU

@4040rec.bsky.socialSep 18, 2026, 8:24 AM

#breastcancer #NICE #NHS #HEOR #Enhertu #AstraZeneca #DaiichiSankyo #Oncology #HER2lowbreastcancer #incurablebreastcancer #NICEFinaldraftguidance #reimbursement #metastaticbreastcancer #NICEcosteffectivenessthreshold #NICErecommendation #CancerDrugsFund #NHScommissioning
zurl.co/eYPtT

@nfbot.bsky.socialSep 7, 2026, 12:33 PM

#Merck #Ezmekly #NHSuse #HEOR #MarketAccess #MerckKGaA #Neurofibromatosis #NF1 #NFItherapy #rarediseases #Reimbursement #NICE #oralMEKinhibitor #plexiformneurofibromas #PN #PNassociatedwithNF1 #paediatrics #MHRA #NICEfinaldraftguidance #paediatricNF1patients

@4040rec.bsky.socialSep 7, 2026, 12:13 PM

#Merck #Ezmekly #NHSuse #HEOR #MarketAccess #MerckKGaA #Neurofibromatosis #NF1 #NFItherapy #rarediseases #Reimbursement #NICE #oralMEKinhibitor #plexiformneurofibromas #PN #PNassociatedwithNF1 #paediatrics #MHRA #NICEfinaldraftguidance #paediatricNF1patients #ReNeutrial #PNlesions
zurl.co/8MUea