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@newsen.bsky.socialOct 1, 2026, 3:18 PM

The Future of Fabry Disease Treatments: Six Therapies to Watch #None #gene_therapy #pharmaceuticals #Fabry_disease

@newsen.bsky.socialSep 21, 2026, 8:42 PM

PTC Therapeutics Completes Acquisition of Novel Gene Therapy for Fabry Disease #United_States #PTC_Therapeutics #Warren #Fabry_disease #ST-920

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