Revolutionary study shows LEAPER 2.0 enabled long-term DMD reversal in monkeys & humans via circ-arRNA-guided exon skipping, spurring hope for treatment! #DuchenneMuscularDystrophy PMID:42269605, Cell 2026, @Cell https://www.cell.com/cell/fulltext/S0092-8674(26)00589-1 #Medsky #Pharmsky #RNA #ASHG 🧪
