@cmri.bsky.socialA child's growing liver has long worked against #genetherapy. #CMRI researchers found a way to repair the faulty gene at its source instead of adding a copy that gets diluted over time. Early results are promising. Full publication here: https://doi.org/10.1016/j.ymthe.2026.06.044
@umasschan.bsky.socialA multidisciplinary UMass Chan research team has received $14.7 million to develop new models and gene therapies for alpha-1 antitrypsin deficiency, a genetic defect which causes severe loss of lung function: https://bit.ly/4cEbJj7
#GeneTherapy @xueumass.bsky.social @rti-umasschan.bsky.social
@drtimos.bsky.social🧬 Gene & Cell Therapy | #RareDiseases 🚀
#LucidQuest delivers sharp insights to help biotechs, investors & BD teams stay ahead in fast-moving markets.
📩 [email protected] or http://dlvr.it/TVQJZZ
#GeneTherapy #CellTherapy #Biotech #DueDiligence #InvestmentInsights
@hearinghealthfn.bsky.social"HearConnex is designed as a multi-regional trial": includes Canada, Australia, and the US hearingreview.com/inside-heari... #keeplistening #genetherapy
@longevitytech.bsky.socialSouth Korean RNA-editing firm enters Eli Lilly’s San Diego innovation hub to speed its precision gene-therapy pipeline toward the clinic.
Link as first comment.
@7islucky.bsky.socialFrom @pbs.org
#SickleCell #Disease is so #Painful that it is normal for its sufferers to have to take the most powerful opioids known to mankind. #GeneTherapy #Broke it. Because it is a disease solely of #Black people I am a bit astonished 😲 #Fascist #Amerikkka
@fiosgenomics.bsky.socialDo you know how bioinformatics analyses support cell and gene therapy research? 🤔Read our blog to find out! 💡
https://www.fiosgenomics.com/bioinformatics-analyses-for-cell-gene-therapy-research/
#cellandgenetherapy #celltherapy #celltherapymanufacturing #genetherapy
@kiki2laro.bsky.social🧬 #China: Two children died in two separate #genetherapy trials
👉Known risks, ethical lapses, inadequate oversight, and, in one case, a death that wasn’t reported until nearly a year late
👉When #innovation outpaces #ethics
www.nature.com/articles/d41...
@drtimos.bsky.socialWhat’s shaping CVC investments for 2025? Key trends: AI/ML, Gene Therapy, and a focus on Immune Disorders & Neurodegenerative Diseases. Curious for more? 📥 Download the full report for insights! http://dlvr.it/TVML6S
#CVC #InvestingInInnovation #VentureCapital #GeneTherapy #AI
@dailybaltic.comGene therapy cuts bad cholesterol by half in single treatment #cholesterol #CRISPR #genetherapy
@drtimos.bsky.social🚀 Big buzz at #ASGCT25: #GeneEditing & #CRISPR headlines, 20% data-driven talk, 85% positive vibes on breakthrough therapies for #DMD & #rarediseases!🧬 Download our full #socialmedia report! http://dlvr.it/TVL5wC #GeneTherapy #SocialListening #LucidQuest
@ASGCTherapy @ESGCT
@wimi-bio-tech.bsky.social#QiheBiotech researchers co-engineered #Bxb1 recognition sites (attB(V111)) and recombinase mutants (V76C/R2Q) to achieve up to 30% CAR gene integration in human cells and 24% stable herbicide-resistance gene insertion in elite rice. 🌾🤖 #Recombinase #GeneTherapy #CropBreeding #PrecisionAg
@4040rec.bsky.social