#BiliaryAtresia is the leading cause of liver transplantation in children. This #LiverAwarenessMonth, we’re highlighting the urgent need for new options for patients and families affected by this rare disease.

Learn more: bit.ly/4ynZ9ME

#RareDisease #RNAEditing #Axiomer

This #LiverAwarenessMonth, we’re raising awareness of #BiliaryAtresia (BA), a rare liver disease that affects newborns and young children.

For more information about BA, visit our website: bit.ly/3VykIN6

#RareDisease #PediatricLiverDisease #Axiomer #RNAEditing #LiverHealth

On Sept 30 at 11a ET join our virtual Investor and Analyst educational event “NTCP Modulation in Biliary Atresia via Liver-Targeted RNA Editing”.

For additional information about the event and to register, visit: www.proqr.com/events

#Axiomer #RNAEditing

Axiomer Insights: Our team published findings in Scientific Reports on preclinical liver models for ADAR-mediated RNA editing. Monica from our research team discusses how model selection can inform translatability for our #Axiomer #RNAEditing platform.

Read the paper here: bit.ly/3UWJLZz

ProQR welcomes Chris Hart as Chief Data & AI Officer and Thomas Wolf as Strategic AI Advisor to the Board. Their appointments support our strategy to apply AI across discovery and development. AX-0811, the first AI-discovered ProQR program is now in clinical trials.

#Axiomer #RNAEditing

Duan et al. propose the comparative RNA editomics analytical framework to prioritize potentially adaptive editing sites using multidimensional evidence, including condition specificity and cross-species evolutionary patterns.
doi.org/10.59717/j.t...
#RNAEditing #adaptation

South Korean RNA-editing firm enters Eli Lilly’s San Diego innovation hub to speed its precision gene-therapy pipeline toward the clinic.

Link as first comment.

#longevity #geroscience #rnaediting #elililly #genetherapy

💡 Interested in light-controlled RNA engineering?

👉 Hanswillemenke et al. use light-controlled RNA-protein conjugates to regulate RNA base editing in living cells.

🔗 brnw.ch/21x5n6k

#RNAEditing #RNATargeting #Photocontrol