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#CysticFibrosis #PrecisionMedicine #Kalydeco #FibroseCística
#MedicinaDePrecisão #Ivacaftor #PrIMR

The U.S. Food and Drug Administration's Experience with Ivacaftor in Cystic Fibrosis. Establishing Efficacy Using In Vitro Data in Lieu of a Clinical Trial
DOI: doi.org/10.1513/anna...