@drtimos.bsky.socialWhat’s shaping CVC investments for 2025? Key trends: AI/ML, Gene Therapy, and a focus on Immune Disorders & Neurodegenerative Diseases. Curious for more? 📥 Download the full report for insights! http://dlvr.it/TVVnNN
#CVC #InvestingInInnovation #VentureCapital #GeneTherapy #AI
@dnanexus.bsky.socialOur team will be at the UC San Diego Gene Therapy Initiative Symposium, 16–17 September in La Jolla.
Schedule time to meet with us to learn how we enable pharma organizations to accelerate their time to insights for early-response results.
@thebabaklab.bsky.socialThe @fda.gov has approved the first therapy for glycogen storage disease type Ia (GSDIa).
Genglycos (pariglasgene brecaparvovec-opnr) received accelerated approval for patients aged 8 years and older.
Link in the comments 👇
@longevitytech.bsky.socialA SIRT6 gene therapy trial in senior beagles hit its primary endpoint, lowering biological age and offering a test bed for human medicine.
Link as first comment.
@drtimos.bsky.social🚀 Big buzz at #ASGCT25: #GeneEditing & #CRISPR headlines, 20% data-driven talk, 85% positive vibes on breakthrough therapies for #DMD & #rarediseases!🧬 Download our full #socialmedia report! http://dlvr.it/TVSzLc #GeneTherapy #SocialListening #LucidQuest
@ASGCTherapy @ESGCT
@wimi-bio-tech.bsky.socialFudan University researchers developed #etBE, an engineered Transformer #BaseEditor with up to 35-fold higher C-to-T editing efficiency that achieved 35.13% in vivo liver editing and a 33% LDL-C reduction in mice without off-target trade-offs. 🧬🤖 #FudanUniversity #GeneTherapy #PCSK9
@sigtrans-sttt.bsky.social#Biologics are broadening therapeutic strategies for cardiovascular disease.
This review highlights advances in #CardiacRegeneration, reverse remodeling, #GeneTherapy, vascular function and lipid modulation.
@wimi-bio-tech.bsky.socialTU Munich researchers used RFdiffusion AI to create synthetic transfer vehicles (STV-C8) that outperform LNPs by >1,000-fold in RNA delivery and achieve in vivo CRISPR editing in pigs. 🧬🤖 #Nature2026 #RNADelivery #RFdiffusion #CRISPR #GeneTherapy #STVC8
@pharmaphorum.bsky.socialRight after reporting encouraging data with its #Dravetsyndrome #genetherapy, #EncodedTherapeutics has raised an impressive $275 million to take the programme into a pivotal trial.
@cmri.bsky.socialA child's growing liver has long worked against #genetherapy. #CMRI researchers found a way to repair the faulty gene at its source instead of adding a copy that gets diluted over time. Early results are promising. Full publication here: https://doi.org/10.1016/j.ymthe.2026.06.044
@umasschan.bsky.socialA multidisciplinary UMass Chan research team has received $14.7 million to develop new models and gene therapies for alpha-1 antitrypsin deficiency, a genetic defect which causes severe loss of lung function: https://bit.ly/4cEbJj7
#GeneTherapy @xueumass.bsky.social @rti-umasschan.bsky.social
@drtimos.bsky.social🧬 Gene & Cell Therapy | #RareDiseases 🚀
#LucidQuest delivers sharp insights to help biotechs, investors & BD teams stay ahead in fast-moving markets.
📩 [email protected] or http://dlvr.it/TVQJZZ
#GeneTherapy #CellTherapy #Biotech #DueDiligence #InvestmentInsights
@hearinghealthfn.bsky.social"HearConnex is designed as a multi-regional trial": includes Canada, Australia, and the US hearingreview.com/inside-heari... #keeplistening #genetherapy
@longevitytech.bsky.socialSouth Korean RNA-editing firm enters Eli Lilly’s San Diego innovation hub to speed its precision gene-therapy pipeline toward the clinic.
Link as first comment.
@7islucky.bsky.socialFrom @pbs.org
#SickleCell #Disease is so #Painful that it is normal for its sufferers to have to take the most powerful opioids known to mankind. #GeneTherapy #Broke it. Because it is a disease solely of #Black people I am a bit astonished 😲 #Fascist #Amerikkka
@fiosgenomics.bsky.socialDo you know how bioinformatics analyses support cell and gene therapy research? 🤔Read our blog to find out! 💡
https://www.fiosgenomics.com/bioinformatics-analyses-for-cell-gene-therapy-research/
#cellandgenetherapy #celltherapy #celltherapymanufacturing #genetherapy
@kiki2laro.bsky.social🧬 #China: Two children died in two separate #genetherapy trials
👉Known risks, ethical lapses, inadequate oversight, and, in one case, a death that wasn’t reported until nearly a year late
👉When #innovation outpaces #ethics
www.nature.com/articles/d41...
@4040rec.bsky.social@drtimos.bsky.socialWhat’s shaping CVC investments for 2025? Key trends: AI/ML, Gene Therapy, and a focus on Immune Disorders & Neurodegenerative Diseases. Curious for more? 📥 Download the full report for insights! http://dlvr.it/TVML6S
#CVC #InvestingInInnovation #VentureCapital #GeneTherapy #AI