Gene therapy can partly restore sight in blind people 👁️🧬
The approach, known as optogenetic therapy, harnesses the technique for turning nerve cells on and off using light that scooped the 2026 Nobel prize in physiology or medicine.

Gene therapy can partly restore sight in blind people 👁️🧬
The approach, known as optogenetic therapy, harnesses the technique for turning nerve cells on and off using light that scooped the 2026 Nobel prize in physiology or medicine.
🧬 Gene & Cell Therapy | #RareDiseases 🚀
#LucidQuest delivers sharp insights to help biotechs, investors & BD teams stay ahead in fast-moving markets.
📩 [email protected] or http://dlvr.it/TVqbST
#GeneTherapy #CellTherapy #Biotech #DueDiligence #InvestmentInsights
Australian researchers are making history using CRISPR viral vectors to permanently correct congenital hearing loss in children, delivering life-changing gene therapy directly to the cochlea.
#GeneTherapy #HearingLoss #Zovintus
[Image by AI]
Sarepta's new data shows Elevidys improved motor function in older boys with Duchenne and produced strong early dystrophin levels in kids as young as 2–3. It's promising news, with liver safety still worth watching. #Duchenne #GeneTherapy #Duchenne #GeneTherapy
ng.investing.com/news/stock-m...
BREAKTHROUGH: Inhaled mRNA base editing & synthetic ceDNA nanoparticles bypass AAV viral packaging limits and immunogenicity to enable redosable, curative genetic medicine! Read our deep dive: url.nextechie.in/Xnc883
#Nextechie #Biotech #GeneTherapy #HealthTech
The story is not only about vector design. It includes patient-derived organoids, animal studies, biodistribution, toxicology, GMP manufacturing, dose selection, and years of regulatory preparation before the first patients can be treated.
New hope for nemaline myopathy type 6 patients: Scientists have restored muscle function by reducing Kbtbd13 gene expression in preclinical studies. Thi… #Genetherapy #Geneticmedicine #Kbtbd13 #Muscledisorder #Nemalinemyopathy #Genetherapy #Geneticmedicine #Kbtbd13 #Muscledisorder #Nemalinemyop…
🧬 Last call! The GfV Workshop on Viral Vectors for Gene Therapy & Vaccination takes place Nov 25-27 in Igls/Innsbruck 🇦🇹
Keynotes by Florian Krammer, Asisa Volz, Patrik Erlman & Ralf Amann.
⏰ Registration closes Wed, Oct 7!
👉 viralvectors.g-f-v.org
Single-Dose CaBP4 Gene Therapy Rewired Adult Dog Retinas and Rebuilt the Synaptic Layer That Never Formed
#dna #dogs #genetherapy #health #healthnews #news #Research #science #scientists #Study
📆First day of the #CGMESA26 ! We look forward to seeing everyone this week.
Don’t miss @genethonfr.bsky.social activities presentation by Imen Mestiri, PhD, Business Development and Licensing Lead October 5th at 9:30 am to 9:45 am, FLW Ballroom F.
What’s shaping CVC investments for 2025? Key trends: AI/ML, Gene Therapy, and a focus on Immune Disorders & Neurodegenerative Diseases. Curious for more? 📥 Download the full report for insights! http://dlvr.it/TVmm1P
#CVC #InvestingInInnovation #VentureCapital #GeneTherapy #AI
Via Euronews: Gene therapy: The breakthrough that inspired Spider-Man | Euronews Tech Talks
www.euronews.com/2026/09/30/g...
#RNATherapy #RNA #GeneTherapy #SpiderMan #HowDoesItWork
🚀 Big buzz at #ASGCT25: #GeneEditing & #CRISPR headlines, 20% data-driven talk, 85% positive vibes on breakthrough therapies for #DMD & #rarediseases!🧬 Download our full #socialmedia report! http://dlvr.it/TVlYyc #GeneTherapy #SocialListening #LucidQuest
@ASGCTherapy @ESGCT
Register now: NIH and HESI Global hybrid workshop on cell and gene therapies!
View details and register: https://ow.ly/EOnh50ZTTgW
#HESIGlobal #CellTherapy #GeneTherapy #Biodistribution #TranslationalResearch #SafetyScience #collaboration
Registration is now open for the next Molecular Therapy Presents webinar, Beyond prevalence: How rare diseases are shaping therapeutic innovation. Learn more and register here today: http://dlvr.it/TVlH1Z
Roche has ended its Huntington's disease gene-silencing program, marking a key shift in neurodegenerative drug development. Meanwhile, ARPA-H launches a new … #ARPAH #Genetherapy #Huntingtonsdisease #Neurodegenerativedisease #Roche #ARPAH #Genetherapy #Huntingtonsdisease #Neurodegenerativedisea…
The Human Genome Project didn’t end genomics—it opened the door.
Its sequence helped fuel #precisionmedicine, #cancergenomics, #genetherapy and #genomeediting.
And it revealed a deeper question:
🧬 How is the genome regulated? Enter the world of #Epigenetics.
#HumanGenomeProject #HGP #Genomics
Gene therapy could transform HAE treatment: https://bit.ly/4mxg8aV
#GeneTherapy #HAETreatment #InnovationInMedicine #RareDiseaseTreatment #MedicalAdvances #AngioedemaNews #Bionews
🧬 Harvard engineers have created a silicon chip that writes DNA sequences using electricity and water—replacing toxic chemicals and enabling portable … #Bioengineering #DNAsynthesis #Genetherapy #Harvardresearch #Microelectronics #Bioengineering #DNAsynthesis #Genetherapy #Harvardresearch #Micr…
First we build the tools,
then they build us.
-Marshall McLuhan
#genetherapy #rna #dna #geneticengineering #artificalintelligence #ai #bio #biotech #biotechnology #stemcells #stemcell #stem
#Genetics #crispr #cloning #genomes #genome #spiderman #medical #health #healthy #genes #tech #news